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Decipher Genomics . Develop Therapeutics
News and Recognition
"Recognition of our global rare disease efforts is a welcome means, rather than a goal"
California, USA | April 15, 2025
"Most Innovative Rare Disease Therapeutic Solutions Provider 2025": Biotechnology and Lifesciences Award
We are glad to share qRare International's recognition by Global Health & Pharma Magazine (GHP). This award further highlights our unwavering commitment to the betterment of rare disease genomics and therapeutics development globally.
Check out the full announcement here.
California, USA | November 03, 2025
"FDA Approves 1st drug for thymidine kinase 2 deficiency, a very rare mitochondrial disease"
We are glad to share with the Thymidine Kinase 2 Deficiency (TK2d) and the broader rare disease communities FDA's approval of the first TK2d-targeted therapy.
This milestone highlights qRare International's continued commitment to serve rare disease families across the world via successful global multi-national collaboration.
Check out the full announcement here.
California, USA | June 24, 2025
"Lenmeldy (atidarsagene autotemcel for individuals with early metachromatic leukodystrophy (MLD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)"
Our latest scientific contribution to the rare disease community is currently published. Check out the newest therapeutics bulletin in 'Genetics in Medicine Open', the official journal of the American College of Medical Genetics and Genomics (ACMG).
Check out the full announcement here.
California, USA | February 17, 2023
"FDA Approves first enzyme replacement therapy for rare alpha-mannosidosis"
We are extremely honored to further share with the alpha-mannosidosis community this amazing news that represents qRare International's key mission of conducting successful international collaborations.
This achievement has made it possible for patients with alpha-mannosidosis of all ages to have a renewed hope for having a targeted treatment.
Check out the full announcement here.
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